Gene therapy, heart failure

The company now says that, during a recent meeting with the FDA, the two parties agreed on some key elements for an ...
The FDA will allow uniQure NV to seek accelerated approval for its Huntington’s disease gene therapy more than doubled the ...
Crucially for the Netherlands-based biopharma company, the FDA has said that the composite Unified Huntington's Disease ...
A lengthy treatment process, coupled with weighty risks for recipients to consider, has resulted in plodding adoption of ...
Monroe Carell was a natural fit to offer the new therapy. Its multidisciplinary DMD Clinic, co-directed by Burnette, Soslow ...
The placenta, or afterbirth, is considered sacred by some cultures, its pivotal role in pregnancy recognized as far back as the raising of Egypt's pyramids. It provides nutrients and oxygen to the ...
Two Saudi Arabian agencies signed on with Vertex Pharmaceuticals to help boost the countr | The Vertex agreement is part of ...
Terry Pirovolakis built a gene therapy to save his son from an ultra-rare disease. Now he has become the first stop and last ...