A new study using gene therapy from the University of Utah reversed the impact of heart failure in pigs. Can it work on ...

Researchers found a genetic therapy that could be used to reverse heart failure. A recent study found that it worked on large ...

Heart failure has historically been irreversible, but a new study suggests that could change. At the University of Utah, ...

Researchers at the meeting reported on long-term activity of commercialized gene therapies and preliminary data on ...

Avidity Biosciences' AOC platform shows promising results for genetic diseases, making it a strong buy with potential upside ...

A study links undetected diabetes in hemochromatosis patients to increased mortality, highlighting the need for early ...

Over the past two decades, awareness has grown about the wide-ranging applications of genomic technologies in human health and beyond.1 This awareness was further heightened during the coronavirus ...

Researchers suggest an application to FDA may be made within the next 12 months, requesting approval to carry out a human clinical trial with the gene therapy.

A new gene therapy can reverse the effects of heart failure and restore heart function in a large animal model.

The FDA will allow uniQure NV to seek accelerated approval for its Huntington’s disease gene therapy more than doubled the ...

SAN DIEGO -- Results from a small single-center study showed that treatment with a gene therapy involving the use of ...

The company now says that, during a recent meeting with the FDA, the two parties agreed on some key elements for an ...